JMML research is sometimes put on hold because orphan disease funding from the government and major non-profit grantmakers is very limited. In order to further our mission of curing this disease, the JMML Foundation has asked researchers into the disease to keep us updated on promising projects that have been written but temporarily shelved due to lack of available funding. These “wish list” research projects, as well as emerging opportunities for novel therapies as identified by researchers, will be listed below as received and reviewed.

Emerging Therapies

• Targeting the granulocyte-macrophage colony-stimulating factor receptor
• Targeting Ras proteins
• Targeting Raf-1 gene expression
• Inhibition of angiogenesis